2020 MSG Annual Meeting

Thank you for a great 2020 MSG Annual meeting!

Thank you to all who participated in the 2020 MSG virtual meeting. If you would like to review the recorded sessions please see the links below.
Friday recorded general session https://youtu.be/mdw-_sRbgC4
Saturday recorded general session https://youtu.be/ztzsL5igp38
Sunday recorded general session https://youtu.be/lPNHuQI37ko

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Accepted Abstracts are posted on the RRNMF Journal at https://journals.ku.edu/rrnmf

2016 MSG Annual Meeting

The 2016 Muscle Study Group annual Meeting was held September 24-26, 2016, at the Snowbird Ski & Summer Resort in Snowbird, UT. Please click on the following links to be directed to the presentation slides, Poster Abstracts, and agenda for the meeting.

Final Agenda

Abstracts: Link to Abstracts

Presentations: Link to Presentations

Sponsors

MSG 2016 Sponsors

2015 MSG Annual Meeting

MSG Attendee Picture

 

The 2015 the Muscle Study Group Annual Meeting took place at its new home in Snowbird, UT at the Snowbird Ski & Summer Resort.

This year’s meeting, titled “Experimental Therapeutics Across the Spectrum of Neuromuscular Disease” was a huge success and brought together members from all across the globe, including pharmaceutical industry, NIH and academic researchers.

Final Agenda

2015 MSG Meeting Final Agenda

Abstracts

Meeting abstracts were published in Muscle & Nerve 2015; 52:S1 (September 2015)

Presentations

The Muscle Study Group has received approval from the authors to publish the following presentations on our website:

An Ounce of Prevention is Worth a Pound of Cure; Michael P. McDermott, PhD

NINDS Funding Opportunities; Glen Nuckolls, PhD

Placebo, History and Impact on Clinical Trials Outcome; Aziz Shaibani, M.D.

Best Practices for Preclinical Research in Neuroscience; Oswald Steward, PhD

Cost of Drugs for Neuromuscular Disorders; Donald B. Sanders, M.D.

Clinical Trials Programs at NIAMS; Tom Cheever, PhD

Sponsors 

The Muscle Study Group wishes to thank the sponsors of the 2015 annual meeting:

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2014 MSG Annual Meeting

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The 2014 Muscle Study Group Meeting took place at the Beaver Hollow Conference Center (Java Center, NY) – September

The meeting, titled “Economic Considerations in the Development of New Treatments for Neuromuscular Diseases” brought together members of the pharmaceutical industry, NIH and academic researchers.

Final Agenda

2014 MSG Meeting Final Agenda

Abstracts

Meeting abstracts were published in Muscle and Nerve 2014;50:S1 (September 2014)

Presentations

The Muscle Study Group has received approval from the authors to publish the following presentations on our website.

Transcriptome Profiling Identifies Key Differences Between Patients with Recessive or Dominant Negative Mutations in Collagen VI Related MyopathiesRussell Butterfield

Complications of Pregnancy in Myotonic DystrophyNicholas Johnson

Funding New Investigators: The Role of the CTSAs Karl Kieburtz

Targeting Mitochondrial Free Radical Production in Aging Skeletal MuscleDavid Marcinek

Outcomes: MDA-NINDS WorkshopJohn Porter

Cataloging FDA’s Flexibility in Subpart H and Orphan Drug ApprovalsFrank Sasinowski

Patient-Reported Outcomes (PROs) in Randomized Clinical Trials (RCTs)Ira Shoulson

MRI in Experimental Muscle TherapeuticsTracey Willis

Sponsors

The Muscle Study Group wishes to thank the sponsors of the 2014 annual meeting:

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NOVARTIS

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walgreens

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2013 MSG Annual Meeting

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The 2013 Muscle Study Group Meeting was held at Lady Margaret Hall, Norham Gardens, Oxford, UK – September 16, 17 and 18.

The meeting was entitled “Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy” and brought together members of the pharmaceutical industry, NIH, FDA and academic researchers.

Final Agenda

2013 MSG Annual Meeting Final Agenda

Abstracts

Meeting abstracts were published in Muscle and Nerve 2013; 48:S1 (September 2013)

Sponsors

The Muscle Study Group wishes to thank the following for their support of the 2013 meeting:

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2012 MSG Annual Meeting

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The MSG held its annual meeting on September 27-29, 2012, at Beaver Hollow Conference Center, Java Center, NY.

The meeting, entitled “Clinical Trial Design and Biomarkers in Neuromuscular Disease,” brought together members of the pharmaceutical industry, NIH, FDA and academic researchers.

The agenda included five major sessions: Clinical Trial Design: Novel Approaches, NIH and Foundation Perspectives, Overview of Biomarkers as Indicators of Therapeutic Efficacy and the FDA’s Perspective, Pathogenesis and Treatment: Recent Discoveries, and Update of Specific Biomarkers as Indicators of Therapeutic Efficacy in Neuromuscular Disease.

Presentations

The Muscle Study Group received permission from the authors to post the following presentations online.

Supporting the Discoveries of TomorrowSanjay Bidichandani

Development and Validation of the MG Composite and MG-QOL15Ted Burns

Adaptive Clinical Trial DesignsScott Evans

Recent Developments in SMAJohn Kissel

Functional MeasuresJackie Montes

Rituxan in Myositis Study – the Tale of a Novel Trial DesignChester Oddis

Outcome Measurements as Clinical BiomarkersSindhu Ramchandren

Electrical Impedance MyographySeward Rutkove

Abstracts

Abstracts for which approval was received to post online are listed below.

Strength and Functional Outcomes in LGMD2a Lindsay Alfano

Frequency and Circumstances of Falls in People with Inclusion Body Myositis in the United KingdomLiz Dewar

Are Sensory Electrodiagnostic Parameters Useful in Differentiating Axonal and Demyelinating Neuropathies?Raghav Govindarajan

Rates of Adverse Events After High Dose IVIG Infusions Do Not Differ Among Patients Receiving 2 Day versus 5 Day Infusions Shafeeq Ladha

ADAPT: Acthar in Dermatomyositis and Polymyositis Treatment RegistryTodd Levine

Johns Hopkins Myositis Center Experience with Inclusion Body MyositisThomas Lloyd

Development of a Virtual Upper Extremity Assessment Tool for Individuals with DMD Across the Lifespan Linda Lowes

Natural History of Sporadic Inclusion Body Myositis — An Observational Longitudinal StudyPedro Machado

Antibody Levels Correlate with Creatine Kinase Levels and Strength in Anti-HMG-CoA Reductase-Associated Autoimmune MyopathyAndrew Mammen

CLCN1 Mutation is Acting as a Modifier Gene in an Italian DM2 Family with Juvenile OnsetGiovanni Meola

MRI Quantification of Abnormal Muscle Water Distribution in Chronic Neuromuscular Diseases: A Sensitive BiomarkerJasper Morrow

Efficacy and Safety of Privigen in Patients with Chronic Inflammatory Demyelinating Polyneuropathy: The PRIMA TrialPatty Riley

Exploring Activity Levels in People with Charcot-Marie-Tooth Disease or Inclusion Body Myositis in Comparison to Healthy ControlsAmanda Wallace

Hereditary Spastic Paraplegia Genetics in the Exome Era: Data on 123 HSP ExomesStephan Zuchner

Sponsors

The Muscle Study Group would like to thank the following sponsors for the 2012 MSG Annual Meeting:

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2011 MSG Annual Meeting

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The MSG held its annual meeting on September 19-21, 2011, at Beaver Hollow Conference Center, Java Center, NY. The meeting was entitled “Translational Research in Neuromuscular Diseases: Diverse Diseases, Convergent Themes.” The meeting brought together members of the pharmaceutical industry and academic researchers.

The agenda included five major sessions: RNA Metabolism as Therapeutic Target in Muscle Disease, RNA Metabolism as Therapeutic Target in Motor Neuron Disease, Government/Foundation Perspectives on NM Themes, Animal Models and Translational Research, and Exercise as a Therapy for NM Disease.

Abstracts

The Muscle Study Group received permission to post the following abstracts online.

Fat Metabolism Syndrome in Patients with DMD Following Low Energy Femur FractureEmma Ciafaloni

Plasma Exchange Complications are Related to the Venous Access RouteJeffrey Guptill

A Prospective, Randomized Controlled Trial of Valproic Acid in Ambulant Adults with SMA: The VALIANT TrialJohn Kissel

Amyloidosis and Exercise Tolerance in AN05 Muscular DystrophyMargherita Milone

MRI Quantification of Lower Limb Muscle Fatty Atrophy: A Potential Outcome Measure in Chronic NM DiseasesJasper Morrow

Identifying the Cause of Phenotypic Variability in a Family with NDMDips Raja Rayan

Sponsors

The meeting was sponsored by:

  • National Institutes of Health, Grant #1R13NS076196-01
  • Muscular Dystrophy Association
  • ISIS Pharmaceuticals
  • PTC Therapeutics
  • Crescent Healthcare, Inc.
  • Genzyme Corporation